Companies

HIV, Oncology, Liver. Key products: Biktarvy, Trodelvy, Livdelzi.

Oncology, I&I, Bone. Key products: Repatha, Prolia, Lumakras.

Rare Disease (CF), Pain, Gene Therapy. Key products: Trikafta, JOURNAVX, Casgevy.

Rare Disease. Key products: Voxzogo, Palynziq, Roctavian.

I&I, Ophthalmology, Oncology. Key products: Dupixent, EYLEA HD, Libtayo.

Neuropsychiatry. Key products: Leqembi, Spinraza, Tysabri.

I&I, Oncology, Neuro. Key products: Humira, Skyrizi, Rinvoq.

Rare Disease (RNAi). Key products: Amvuttra, Onpattro, Givlaari.

Vaccines, Oncology, Rare. COVID/RSV vaccines platform.

Neuro, Cardio, Rare. Key products: SPINRAZA, WAINUA.

Liver, Cardio, Pulmonary. Key product: Plozasiran.

Rare Disease (Gene Editing). Key product: Casgevy.

Neuromuscular, Cardio. Lead: del-desiran (Ph3).

Rare Disease (Gene Editing). Lead: BEAM-101 (Ph1/2).

Rare Disease (Gene Editing). Lead: NTLA-2001 (Ph3).

Cell Engineering platform for hypoimmune cells.

Prime Editing platform. Lead: PM359 (Ph1).

AAV gene therapy platform. Multiple programs.

Rare - Liver. Key product: Livmarli.

Neuropsychiatry. Key products: Vivitrol, Aristada.

Rare - Lysosomal. Key products: Galafold, Pombiliti.

Drug Delivery. ENHANZE royalties.

Rare - Dermatology. Key product: Vyjuvek.

Cardiovascular. Key product: Myqorzo.

Dx - Oncology. Key product: Galleri.

Oncology, I&I. Key products: Jakafi, Opzelura.

Rare Disease. Key products: Translarna, Evrysdi royalties.

Oncology. Key product: Cabometyx.

Dx - Oncology. Key products: Cologuard, Oncotype DX.

Dx - Oncology, Prenatal. Key products: Signatera, Panorama.

I&I (MS). Key product: Briumvi.

Rare - PAH. Key product: Tyvaso DPI.

Rare - Nephrology. Key product: Filspari.

Metabolic - MASH. Key product: Rezdiffra.

Neuropsychiatry. Key product: Ingrezza.

Neuropsychiatry. Key products: Nuplazid, Daybue.

I&I (Immunoglobulins). Key product: ASCENIV.

Rare - Pulmonary. Key products: Arikayce, Brinsupri.

Ophthalmology. Key product: Syfovre.

Rare Disease. Key products: Crysvita, Evkeeza.

Neuropsychiatry. Key product: Firdapse.

Dx - Oncology. Key products: Decipher, Afirma.

Vaccines. COVID vaccine.

Nephrology, GI. Key products: Ibsrela, Xphozah.

Rare - Hematology. Key product: Pyrukynd.

Vaccines. Key product: Heplisav-B.

Regenerative. Key products: MACI, Epicel.

Diabetes, Pulmonary. Key products: Afrezza, Tyvaso DPI.

Rare Disease. Key product: Orladeyo.

Dx - Transplant. Key product: AlloSure.

Oncology. Key product: Amtagvi.

Allergy. Key product: Neffy.

Oncology. Key product: Rytelo.

Vaccines/Biodefense. Biodefense products.

I&I. Key product: Rezlidhia.

Dx - Oncology. Key product: BRACAnalysis.

Rare - DMD. Key product: Elevidys.

Regenerative. Key products: AmnioFix, EpiFix.

GI. Linzess royalties.

Oncology (RAS). Lead: Daraxonrasib (Ph3).

Oncology (HER2). Lead: Gedatolisib (Ph3).

Oncology (Oncolytic). Lead: CG0070 (Ph3).

Oncology (CAR-T). Lead: Anitocabtagene (Ph2).

Oncology (TKI). Lead: NVL-520 (Ph2).

Oncology (PD-1). Lead: Ivonescimab (Ph3).

Oncology (Synth Lethality). Lead: Darovasertib (Ph3).

Oncology (Menin). Lead: Revumenib (BLA).

Oncology (IL-15). Key product: Anktiva.

Oncology (Antibodies). Lead: IMM-1-104 (Ph1).

Oncology (Synth Lethality). Lead: TNG908 (Ph2).

Oncology (T-cell Engager). Lead: JANX007 (Ph1).

Oncology (IO). Lead: Mupadolimab (Ph2).

Oncology (IO). Lead: Domvanalimab (Ph3).

Oncology. Lead: ORIC-114 (Ph2).

Oncology (Pediatric). Key product: Tovorafenib.

Oncology (Gene Therapy). Lead: PRGN-3005 (Ph1).

Oncology (Degrader). Lead: NX-2127 (Ph1).

Oncology (Probody). Lead: CX-904 (Ph1).

Oncology (Menin). Lead: Ziftomenib (Ph3).

Oncology (PI3Ka). Lead: Zovegalisib (Ph3).

Oncology (Degrader). Lead: MRT-2359 (Ph1).

Oncology (RAS). Lead: Naporafenib (Ph2).

Oncology (Bispecific). Lead: Vudalimab (Ph2).

Oncology (ER). Lead: Palazestrant (Ph3).

Oncology (Oncolytic). Lead: RP1 (Ph2).

Oncology (Bispecific). Lead: BCA101 (Ph2).

Oncology (IO). Lead: CTX-009 (Ph2).

Oncology (RAF/MEK). Lead: Avutometinib (Ph3).

Oncology. Lead: CLN-978 (Ph1).

Oncology. Lead: ARRY-440 (Ph2).

Oncology. Lead: IMM-1-104 (Ph1).

Oncology (TKI). Lead: TYRA-300 (Ph2).

I&I, Hematology. Lead: Rusfertide (Ph3).

I&I (Dermatology). Lead: Roflumilast (Ph3).

I&I (Degrader). Lead: KT-474 (Ph2).

I&I (FcRn). Lead: IMVT-1402 (Ph3).

I&I (Dermatology). Lead: APG777 (Ph2).

I&I (Thyroid Eye). Lead: VRDN-003 (Ph3).

I&I (Complement). Lead: DNTH103 (Ph2).

Hematology. Lead: Bitopertin (Ph3).

I&I (KIT). Lead: Barzolvolimab (Ph3).

I&I. Lead: Zelnecirnon (Ph2).

I&I (IBD). Lead: SPY001 (Ph2).

I&I (PD-1 Agonist). Lead: Rosnilimab (Ph3).

I&I (Dermatology). Lead: ORKA-001 (Ph2).

I&I (Pulmonary). Lead: UPB-101 (Ph2).

I&I (Complement). Lead: ANX005 (Ph3).

I&I. Lead: INBRX-101 (Ph2).

I&I (Hematology). Lead: KER-050 (Ph2).

Rare Disease, Cardio. Key product: Acoramidis (Approved).

Multiple (Holding Co). Multiple Vants.

Rare - Neuromuscular. Lead: Apitegromab (Ph3).

Rare - Metabolic (Obesity). Key product: Setmelanotide.

Rare - Mast Cell. Lead: Bezuclastinib (Ph3).

Rare - Neuromuscular. Lead: DYNE-101 (Ph2).

Rare - Gene Therapy. Lead: AMT-130 (Ph1/2).

Rare - PWS. Lead: DCCR (Ph3).

Rare - Gene Therapy. Lead: TSHA-120 (Ph1/2).

Rare - HAE. Key product: Sebetralstat (Approved).

Rare - Dermatology. Lead: PV-10 (Ph3).

Rare - Ophthalmology (Gene Therapy). Lead: 4D-150 (Ph2).

Rare - Gene Therapy. Lead: LX1001 (Ph1/2).

Rare - Pulmonary. Lead: Molgramostim (Ph3).

Neuropsychiatry (Epilepsy). Lead: Ulixacaltamide (Ph3).

Neuropsychiatry (Neurodegeneration). Lead: Tividenofusp alfa (BLA).

Neuropsychiatry (Genetic). Lead: STK-001 (Ph2).

Neuropsychiatry (Multiple). Lead: Troriluzole (Ph3).

Neuropsychiatry (Alzheimers). Lead: Blarcamesine (Ph3).

Neuropsychiatry (Amyloid). Lead: Birtamimab (Ph3).

Metabolic (Obesity). Lead: VK2735 (Ph3).

Cardiovascular (HTN). Lead: Lorundrostat (Ph2).

Cardiovascular. Lead: SIO-2007 (Ph1).

Metabolic (Obesity). Lead: Pemvidutide (Ph2).

I&I, Oncology. Lead: Seralutinib (Ph3).

Nephrology (Anemia). Key product: Vadadustat.

Metabolic (Hypoglycemia). Lead: RZ358 (Ph3).

Nephrology (IgAN). Lead: Atacicept (Ph3).

Ophthalmology (Retinal). Lead: Tarcocimab (Ph3).

Infectious Disease. Lead: Elebsiran (Ph2).

Infectious Disease. Lead: VYD222 (Ph2).

Infectious Disease (HBV). Lead: Imdusiran (Ph2).

Vaccines. Lead: VAX-31 (Ph3).

Synthetic Biology. Synthetic DNA platform.

AI Drug Discovery. AI platform.

AI Drug Discovery. AI antibody platform.